Scientific Resources
Selected scientific publications, books, and research contributions from Exir Gene team members and collaborators across gene therapy
Research Publications
Book
September 16, 2026
Gene Therapy in Neurodegenerative Disorders
Vahid Mansouri, Maryam Bemanalizadeh
May 2026
Intravitreal rAAV2.7m8 delivery of a high-affinity VEGF decoy receptor suppresses laser-induced choroidal neovascularization in pigmented rats
Vahid Mansouri, Maryam Bemanalizadeh, Naser Ahmadbeigi
May 2026
Intratumoral AAV2-mediated VEGF blockade limits metastatic dissemination in an immunocompetent breast cancer model
Vahid Mansouri, Maryam Bemanalizadeh, Naser Ahmadbeigi
May 2026
Integrating AAV-SMN1 gene transfer with SMN2 splicing modifiers in spinal muscular atrophy: an updated real-world and trial evidence
Maryam Bemanalizadeh, Vahid Mansouri
August 29, 2025
Combination therapies in spinal muscular atrophy: a systematic review
Maryam Bemanalizadeh, Leida Heidary, Mohammad Sedigh Dakkali, Shiva Hadizadeh, Naser Ahmadbeigi, Morteza Heidari, Gholamreza Zamani, Mahmoudreza Ashrafi, Vahid Mansouri
June 16, 2025
Long-Term Safety and Efficacy of AAV9 Vectors Expressing Human SMN1 Gene: A Preclinical Study
Vahid Mansouri, Maryam Bemanalizadeh, Naser Ahmadbeigi, Ramin Shakeri, Hiva Saffar
September 25, 2024
Beyond numbers: a call to action for accurate estimation of spinal muscular atrophy in the Middle East and North Africa region
Maryam Bemanalizadeh, Vahid Mansouri
February 6, 2023
The first report of Iranian registry of patients with spinal muscular atrophy
Vahid Mansouri, Morteza Heidari, Maryam Bemanalizadeh, Reza Azizimalamiri, Shahriar Nafissi, Masood Ghahvechi Akbari, Mohammad Barzegar, Ali Reza Moayedi, Reza Shervin Badv, Mahmood Mohamadi, Ali Reza Tavasoli, Susan Amirsalari, Ali Khajeh, Soroor Inaloo, Farzad Fatehi, Sareh Hosseinpour, Meisam Babaei, Seyed Ahmad Hosseini, Seyyed Mohammad Mahdi Hosseiny, Afshin Fayyazi, Firoozeh Hosseini, Mehran Beiraghi Toosi, Nahid Khosroshahi, Homa Ghabeli, Habibeh Nejad Biglari, Simin Khayatzadeh Kakhki, Seyed Hossein Mirlohi, Elham Bidabadi, Bahram Mohammadi, Abdolmajid Omrani, Mostafa Sedighi, Mohammad Vafaee-Shahi, Maryam Rasulinezhad, Seyyed Mohamad Hoseini, Mojtaba Movahedinia, Zahra Rezaei, Parviz Karimi, Hossein Farshadmoghadam, Saeed Anvari, Omid Yaghini, Jafar Nasiri, Gholamreza Zamani, Mahmoud Reza Ashrafi
May 2025
Short-Term Hurdles, Long-Term Promise: AAV9-SMN1 Gene Therapy for SMA
Vahid Mansouri, Maryam Bemanalizadeh, Farzaneh Jamshidi, Ramin Shakeri, Hiva Saffar, Naser Ahmadbeigi
May 2025
Comparative Analysis of Transgene Expression of Neurotropic AAV Serotypes and Their Potential in Combination Treatments
Vahid Mansouri, Maryam Bemanalizadeh
May 2025
Over a Decade of Gene Therapy Trials: Evolution from 2010 to 2025
Maryam Bemanalizadeh, Vahid Mansouri
