Publications

Scientific Resources

Selected scientific publications, books, and research contributions from Exir Gene team members and collaborators across gene therapy

Research Publications

Book
September 16, 2026

Gene Therapy in Neurodegenerative Disorders

Vahid Mansouri, Maryam Bemanalizadeh

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May 2026

Intravitreal rAAV2.7m8 delivery of a high-affinity VEGF decoy receptor suppresses laser-induced choroidal neovascularization in pigmented rats

Vahid Mansouri, Maryam Bemanalizadeh, Naser Ahmadbeigi

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May 2026

Intratumoral AAV2-mediated VEGF blockade limits metastatic dissemination in an immunocompetent breast cancer model

Vahid Mansouri, Maryam Bemanalizadeh, Naser Ahmadbeigi

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May 2026

Integrating AAV-SMN1 gene transfer with SMN2 splicing modifiers in spinal muscular atrophy: an updated real-world and trial evidence

Maryam Bemanalizadeh, Vahid Mansouri

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August 29, 2025

Combination therapies in spinal muscular atrophy: a systematic review

Maryam Bemanalizadeh, Leida Heidary, Mohammad Sedigh Dakkali, Shiva Hadizadeh, Naser Ahmadbeigi, Morteza Heidari, Gholamreza Zamani, Mahmoudreza Ashrafi, Vahid Mansouri

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June 16, 2025

Long-Term Safety and Efficacy of AAV9 Vectors Expressing Human SMN1 Gene: A Preclinical Study

Vahid Mansouri, Maryam Bemanalizadeh, Naser Ahmadbeigi, Ramin Shakeri, Hiva Saffar

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September 25, 2024

Beyond numbers: a call to action for accurate estimation of spinal muscular atrophy in the Middle East and North Africa region

Maryam Bemanalizadeh, Vahid Mansouri

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February 6, 2023

The first report of Iranian registry of patients with spinal muscular atrophy

Vahid Mansouri, Morteza Heidari, Maryam Bemanalizadeh, Reza Azizimalamiri, Shahriar Nafissi, Masood Ghahvechi Akbari, Mohammad Barzegar, Ali Reza Moayedi, Reza Shervin Badv, Mahmood Mohamadi, Ali Reza Tavasoli, Susan Amirsalari, Ali Khajeh, Soroor Inaloo, Farzad Fatehi, Sareh Hosseinpour, Meisam Babaei, Seyed Ahmad Hosseini, Seyyed Mohammad Mahdi Hosseiny, Afshin Fayyazi, Firoozeh Hosseini, Mehran Beiraghi Toosi, Nahid Khosroshahi, Homa Ghabeli, Habibeh Nejad Biglari, Simin Khayatzadeh Kakhki, Seyed Hossein Mirlohi, Elham Bidabadi, Bahram Mohammadi, Abdolmajid Omrani, Mostafa Sedighi, Mohammad Vafaee-Shahi, Maryam Rasulinezhad, Seyyed Mohamad Hoseini, Mojtaba Movahedinia, Zahra Rezaei, Parviz Karimi, Hossein Farshadmoghadam, Saeed Anvari, Omid Yaghini, Jafar Nasiri, Gholamreza Zamani, Mahmoud Reza Ashrafi

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May 2025

Short-Term Hurdles, Long-Term Promise: AAV9-SMN1 Gene Therapy for SMA

Vahid Mansouri, Maryam Bemanalizadeh, Farzaneh Jamshidi, Ramin Shakeri, Hiva Saffar, Naser Ahmadbeigi

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May 2025

Comparative Analysis of Transgene Expression of Neurotropic AAV Serotypes and Their Potential in Combination Treatments

Vahid Mansouri, Maryam Bemanalizadeh

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May 2025

Over a Decade of Gene Therapy Trials: Evolution from 2010 to 2025

Maryam Bemanalizadeh, Vahid Mansouri

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